Casgevy is the first CRISPR-based medicine to be approved for use in the United States #CheckRare #BetaThalassemia #Casgevy checkrare.com/fda-approves-c…

#Casgevy why is the amount of fetal hemoglobin drastically lower in sickle cell vs beta-thalassemia population? Are gamma-globin/sickle cell globin heterodimers not formed/measured? Editing levels are very similar. $CRSP $VRTX

.@ChildrensPhila researchers demonstrated improved quality of life for #sicklecelldisease patients with recurrent vaso-occlusive crises. The findings provide the complete details of the trial leading to @US_FDA approval of #Casgevy in Dec. 2023. bit.ly/3Uw3SLA

Does anyone know if $VRTX will receive the entire $2.2 million for #Casgevy or will a portion be paid to Authorized Treatment Centers for conducting the transplant? My assumption is that Vertex gets the entire amount and the medical center charges separately for conducting the…

In this interview with @AlexWestchester and @KevinADavies, Jim Wilson remarks on the FDA approval of the first #CRISPR-based cell therapy, #Casgevy, and provides an outlook for the cell and gene therapy commercial space. Read the full interview: liebertpub.com/doi/10.1089/ge…

Approved product for 2 blood indications … $CRSP couple of billion in cash … opportunity … way oversold #Casgevy

URGENT! 5pm TODAY is the DEADLINE for #NICE Consultation, following their rejection of #Casgevy, a cureative #treatment for Sickle Cell Disorder. Please submit your comments to: 📧 lnkd.in/eg2zDJdj #NICE #consultation #SickleCell #haveyoursay #comment #treatment

In today's Real Physician Reacts episode, we delve into a groundbreaking development in the treatment of sickle cell disease. bit.ly/3TuW9xt?utm_ca… #RealPhysicianReacts #SickleCellDisease #GeneEditingTherapy #Casgevy

Casgevy is the first CRISPR-based medicine to be approved for use in the United States #CheckRare #BetaThalassemia #Casgevy checkrare.com/fda-approves-c…

Jennifer Doudna – Seeking to Improve the World with CRISPR oligotherapeutics.org/jennifer-doudn… #ots #CRISPR #CRISPRCas9 #genome #diseasetreatment #currentresearch #currentscience #science #chemistry #casgevy #InnovativeGenomicsInstitute #danahar #dna #editdna #snipdna #jenniferdoudna

$BLUE 4Q result. 1st Lyfgenia patient start “imminent” and has "multiple enrolments" at "multiple treatment centres”. Revenue recog happens at infusion, not cell collection This could translate into similar news for $CRSP $VRTX #CASGEVY hopefully confirming strong patient demand.

In today's Real Physician Reacts episode, we delve into a groundbreaking development in the treatment of sickle cell disease. youtu.be/r7pshTpGbGA?ut… #RealPhysicianReacts #SickleCellDisease #GeneEditingTherapy #Casgevy

In today's Real Physician Reacts episode, we delve into a groundbreaking development in the treatment of sickle cell disease. bit.ly/3TuW9xt?utm_ca… #RealPhysicianReacts #SickleCellDisease #GeneEditingTherapy #Casgevy

It's been nearly four months since the FDA's historic Dec. 8 approval of Vertex-CRISPR's #Casgevy and bluebird bio's #Lyfgenia—the first cell-based #genetherapies approved for #sicklecelldisease. How are the rollouts of these expensive treatments going? biospace.com/article/analys…

🚀Watch our new video featuring Jimi Olaghere as he discusses his firsthand experience and the profound impact of the pioneering approval of Casgevy, the US' first CRISPR therapy. hubs.ly/Q02qKG-40 #Casgevy #SickleCellAwareness #CRISPRTherapeutics [Video Link] 🎥✨

NEW TREATMENT FOR SICKLE CELL REJECTED On the 14th March @NICEComms published it’s draft decision NOT to recommend #Casgevy for NHS funding. #SickleCell HAVE YOUR SAY ' NICE Consultation on a CURE for Sickle Cell - YouTube youtube.com/watch?v=E20-z3…

Casgevy is the first CRISPR-based medicine to be approved for use in the United States #CheckRare #BetaThalassemia #Casgevy checkrare.com/fda-approves-c…

“ #Casgevy, a cell-based gene therapy, is approved for the treatment of sickle cell disease in patients 12 years of age and older with recurrent vaso-occlusive crises. Casgevy is the first FDA-approved therapy utilizing CRISPR/Cas9, a type of genome editing technology.”

“The Power of Precision” One gene .. One edit .. One time! #Casgevy #GeneTherapy #SaudiArabia #Riyadh