Grace Pavlath @GPavlathScience

Vice President Translational Research Solid Biosciences , #Gene Therapy, #Neuromuscular, #RareDisease Joined May 2015

Tweets

149
Followers

227
Following

129
Likes

129

Barry Byrne @barrybyrne1

5 years ago

Bo Cumbo jumps from the top commercial post at Sarepta to the helm of a gene therapy startup with some influential backers, big plans and $107M – Endpoints News endpts.com/bo-cumbo-jumps…

1 1 7 0 0

Sad day for the muscle community with the passing of Prof. David Yaffe from our department @WeizmannScience David (born in 1929) has pioneered culture methods for muscle stem cells including the famous C2 cells.

0 22 92 0 0

Download Image

Brian Tyler Cohen @briantylercohen

6 years ago

The Trump campaign seriously just issued a cease and desist for this ad so I'm doing my part and sharing it as widely as humanly possible.

2K 53K 79K 0 1K

Download Video

Alison Lynch-Miller @AlisonLynchMil1

6 years ago

#LetTheScientistsLead If this was a war and the doctors took over the planning, would that make any damn sense? Medical professionals are merely fodder in Trump’s mismanagement. Let’s stand up and say enough, LetTheScientistsLead!

0 3 2 0 0

Katie Baca-Motes @BacaMotes

6 years ago

“Doctor groups are recommending testing and isolation for people who lose their ability to smell and taste, even if they have no other symptoms.” nytimes.com/2020/03/22/hea…

6 144 199 0 10

Grace Pavlath @GPavlathScience

6 years ago

Fascinating implications of chimerism after bone marrow transplant for forensics apple.news/AFw2GKwlkTy6E-…

0 0 0 0 0

Lynn O’Connor Vos @lynnvos

7 years ago

Very interesting read given #genetherapy #geneediting conversations had at yesterday's #MDAconference n.pr/2V4jNCY #CRISPR #Cancer

0 3 2 0 1

Grace Pavlath @GPavlathScience

7 years ago

Speech may become an important outcome measure in future clinical trials in ALS. Great talk by Jeremy Shefner at #MDAConference #als

0 2 5 0 0

Lynn O’Connor Vos @lynnvos

7 years ago

MDA National Ambassadors Justin, Tana and Faith tried out the new @Microsoft adaptive xbox controller - a 1st xbox experience for Faith. Justin, a strategic and steady driver in the game, mentioned excitement for the ability to customize the controller so anyone can make it work.

1 9 14 0 0

Download Image

Lynn O’Connor Vos @lynnvos

7 years ago

Dr. Janet Woodcock at the #MDAconference @US_FDA

STAT @statnews

7 years ago

Dr. Janet Woodcock at the #MDAconference @US_FDA

0 1 2 0 0

0 4 3 0 0

Dr. Jodi Wolff @drjodiwolff

7 years ago

Fantastic morning ⁦@MDAorg⁩ learning about congenital muscle diseases with Jim Dowling, Reghan Foley & Carsten Bonneman #MDAconference #coll6 #mtm1 #myotubularmyopathy #cmd

0 5 9 0 0

Download Image

Grace Pavlath @GPavlathScience

7 years ago

Lindsay Alfano of @nationwidekids reminds us that selection of outcome measures is not “one-size-fits-all” - we must continue to re-evaluate the outcome as treatments emerge & ‘natural history’ is redefined. Great Outcome Measures talk at #MDAConference

0 2 5 0 0

Grace Pavlath @GPavlathScience

7 years ago

In yesterday's session on Gene–Targeting Therapies, Dr Robert Brown at the UMass Med School shared progress of a pilot human clinical trial using a gene-targeting therapy for a common mutation in #ALS. #MDAconference

0 4 11 0 0

Lynn O’Connor Vos @lynnvos

7 years ago

We at MDA are truly honored to receive the @ASGCTherapy Sonia Skarlatos Public Service Award for significant contribution to gene and cell therapy. Congrats to our entire Scientific team here @MDAorg @GPavlathScience @AHaidetPhillips @LOrlandoScience @Hagerty_Laura #GeneTherapy

0 11 25 0 0

Download Image

Laura Hagerty @Hagerty_Laura

7 years ago

Kicking off the 2019 MDA Clinical and Scientific Conference with a meeting of the MDA Care Center Director physicians. Great discussion underway with the docs trading learnings from across their centers. @MDAorg

0 3 13 0 0

Download Image

Grace Pavlath @GPavlathScience

7 years ago

Fantastic kick off to the #MDAConference! Today's MDA Scholars session invited 4 early stage scientists to present their research on neuromuscular diseases -- research made possible with Development Grants from @MDAorg.

0 1 9 0 0

Grace Pavlath @GPavlathScience

7 years ago

So excited to see an innovative collaboration between @amicusrx and @PennMedicin,e which will explore novel gene therapy approaches for treating rare metabolic diseases including #Pompe, #Fabry, and #CDKL5! #RareCompany [ir.amicusrx.com/press-releases]