Sounds like an “arduous and treacherous path” going forward for VP employment-maybe he can get a retirement job with STAT as an “anonymous source” $SRPT
V Prasad, promenaded out the door-Farkas Farces & you can go fishing together in early retirement-sorry but you are on the wrong side of drug development & PT choice for rare DZ.
$SRPT step up & be open and honest as possible with all in this space!
Thank you again WSJ for being on the right side of drug development for rare dz and patient choice! Your voice is appreciated in this space! $SRPT wsj.com/opinion/fda-re…
$SRPT glad ambulatory patients/families get to make the choice!! Co must provide all information it can-benefits and potential complications so DMD families are empowered to make best choices for themselves!
$SRPT a Friday after hours, vague, clickbait announcement by the FDA of an “investigation” is no way to run a professional, credible, information driven agency. Pathetic.
“A desperate parent has more standing than a bureaucratic panel” or I would add a dictatorial Prasad. Plenty of questions for both FDA and $SRPT. Hope their is humility from both and a way to keep this therapy available
“A desperate parent has more standing than a bureaucratic panel” or I would add a dictatorial Prasad. Plenty of questions for both FDA and $SRPT. Hope their is humility from both and a way to keep this therapy available
$SLDB $RGNX $SRPT all GT affected by $SRPT fall. Not sure how Co compare but it will be a long road for DMD GT considering reg environment & sentiment. All risk liver tox. Combo of correct study endpoints & prophylactic regimen-may have to wait until change in FDA for success
Regardless of the Co missteps-any there have been plenty; what does the DMD community say about GT TX from $SRPT, and the Co communication with them. Scientific evidence and their opinion is really all that should matter here.
$SRPT did the “media” trumpet the 2 year E data set this winter or did that not fit their narrative? It’s time for all the cards to be put on the table, all info that can be openly, voluntarily shared. How are phase 1 fairing this many years out?
$SRPT always wondered why “enhanced safety protocols” not implemented (perhaps for both amb/non-amb) after 1st SAE what are the drawbacks, complications , side effects? It will always be difficult to predict who or why compromised before TX. Safety greatest risk to this tech.
$SRPT is a mess, science backs TX for amb-patients/parents deserve choice. As an investor exited after 1st SAE, Co action, leadership, communication needs “improvement.” FDA, “media” shorts on wrong side. Wish all DMD and LGMD families the best will continue to support as able.
$SRPT X full of “short seller trash post & bots.” Miss the days of true investors, science seekers, pt activist. Good luck to all who care, whose hearts and minds are motivated by compassion, hope, and promise of better science leading to better lives.
Sad news for $SRPT and GT class as a whole-unfortunately not good for any GT co or future GT from $SRPT. Viral load on “compromised patients” too much-Just sad gut punch to hope and promise for many. Thoughts and prayers with DMD families and rare dz space
Unfortunately “good science” does not = “good company”, a “good company” does not = “a good stock”. Always thought $SRPT had good science, not sure about the rest anymore. LGMD with full length protein needs to get to market. Future of all GT affected by $SRPT success/failure
1st awesome news on LGMD $SRPT! Good sign for rare dz and GT! But I guess I don’t understand this “quiet period”-is it over? What can Co say, not say? Just don’t get the radio silence on DMD
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