Friend to most, foe to Duchenne @JenniferHandt
Mother of boys and other animals. Writer. Ideas-seeker. Love books + real talk. Red Sox Nation lifer. Duchenne warrior: https://t.co/OOrB4PPSTL Joined January 2011-
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The FDA accelerated approval pathway works — but it isn't flawless - STAT statnews.com/2024/04/23/acc…
"These cells, derived from human pluripotent stem cells, have shown promise in preclinical studies for their ability to regenerate damaged skeletal muscle." Regeneration: Do we dare to dream? This sounds hugely promising @ParentProjectMD @DuchenneUK
"These cells, derived from human pluripotent stem cells, have shown promise in preclinical studies for their ability to regenerate damaged skeletal muscle." Regeneration: Do we dare to dream? This sounds hugely promising @ParentProjectMD @DuchenneUK
We are at a decisive moment where #Duchenne is just beginning to evolve from a death sentence to a manageable chronic condition. The @US_FDA #acceleratedapproval pathway is key to seizing this moment and saving lives. More in @statnews today.
We are at a decisive moment where #Duchenne is just beginning to evolve from a death sentence to a manageable chronic condition. The @US_FDA #acceleratedapproval pathway is key to seizing this moment and saving lives. More in @statnews today.
Thanks for an eminently reasoned defense of #acceleratedapproval @steveusdin1. As in oncology, the rare disease community knows AA is a lifeline (literally). In fact, that “controversial” #Duchenne therapy just demonstrated 5.5 yr+ survival. I dare say it proves your point!
Thanks for an eminently reasoned defense of #acceleratedapproval @steveusdin1. As in oncology, the rare disease community knows AA is a lifeline (literally). In fact, that “controversial” #Duchenne therapy just demonstrated 5.5 yr+ survival. I dare say it proves your point!
What. More. Do. People. Need. To. See.
Exondys 51 treatment for up to eight years extended survival in DMD patients over a wide range of ages, a long-term study found. buff.ly/4bd6hk7 #MuscularDystrophyNews #MuscularDystrophy
Live in CT? Please help me make some noise for this bill to add Duchenne to our standard health screening for all newborns. There is no reason for diagnostic guessing games in 2024. Every child should get timely treatment. engage.parentprojectmd.org/2024-ct-nbs?fb…
cc: Accelerated Approval critics. 💥
cc: Accelerated Approval critics. 💥
Over 60 leading experts in genetics, pediatrics, neurology, and public health advocates have authored a consensus statement in support of implementing #Duchenne newborn screening. parentprojectmd.org/60-experts-uni…
Differently abled is the new black. Good night moon.
We’re calling on the MHRA to quickly approve Duchenne muscular dystrophy treatment givinostat. Our co-founder and Chief Executive, Emily Reuben OBE, shares her painful personal experience to highlight the need for its quick approval.🔗 dailymail.co.uk/health/article…
This is one of the most wholesome moments I’ve seen in a long time. This young girl brought to tears after @Kamillascsilva signs her ‘Everyone watches women’s sports’ sweatshirt. She has a @dawnstaley autograph on there too!! Got choked up shooting this 🥹 @GamcockWBB
Dick Cheney @DickCheney18
1 Followers 10 Following
KARTHICK K @karthickk1989
28 Followers 172 Following I'm devotional addicater,and motivated myself. I want to enjoy my life with my bike for travel anywhere on that time hearing songs
Chris Young @CYoung98506
6 Followers 240 Following my new album Young Love & Saturday Night is out now!
Joe @Gentocj
1 Followers 52 Following Equity market consultant. Technical Analysis Trader with over 25 years of experience. #Biotech Deep dive research.Bitcoin Trading Analyst @ChimeraResearch
Critical Cupcake 🌈.. @CriticalCupcake
110K Followers 116K Following Science, Comedy, Left, LGBTQ+, Atheist, #Resistance ChronicPain, PolyBiPan, Queer, Anti-Religious-Harm + Bigotry, Everyone is an idiot sometimes, esp. me ;)
Fran Jones @Frannie_JoJo
7K Followers 7K Following Here to save our rights!! #ProChoice #VoteBlue, #ConnectBlue, #FBR, #LGBTQIA+, #Resist, #StrongerTogether NO DMs!
Joe @1Gantosj
44 Followers 1K Following Equity market consultant. Technical Analysis Trader with over 25 years of experience. #Biotech Deep dive research. Biotech Trading Analyst @ChimeraResearch
WILL–PARFITT @will_parfitt787
5 Followers 265 Following Catch me if you can. Property investor 🏠x4 Founding Father @magicmenaustralia WORLD TOUR TICKETS 🌍👇🏾
Jared Friedman @haydenzadams45
96 Followers 5K Following founder, techno-optimist, college dropout partner at @ycombinator.
Alieu Manka @MankaAlieu88410
92 Followers 3K Following
Elijah Stacy @Elijahjstacy
379 Followers 250 Following Author, Public Speaker, and Founder of Destroy Duchenne. Media/bookings: [email protected]. Get my new book now 👇
Connecticut Examiner @ctexaminer
3K Followers 4K Following Connecticut's award-winning source for state and local news -- 235,000 readers and counting. Write to us: [email protected]
Meiko @meikobauchman
213 Followers 1K Following bad ass mom, wife, former international woman of mystery, Star Wars and HP fan.
Institute for Gene Th.. @gene_therapies
2K Followers 415 Following Gene therapy is transforming how we treat diseases. But today’s healthcare system can’t realize its potential. We’re changing that.
Dawn Kirk @DawnzkKirk
17 Followers 670 Following Lured the best beauties from all US states 😇 Ready for private meetings See nude photos before a date! Watching this https://t.co/JFIEoVVwnn
Eileen @eileen_wigfall9
860 Followers 3K Following
Howard Ron @HowardRon1
20 Followers 62 Following
Elida @elida_schroder
171 Followers 3K Following
MarkSharkKing @MarkSharkKing
111 Followers 643 Following
walid bitam @walidbitam7
27 Followers 407 Following
brian nicholoff @Bpn9211Brian
102 Followers 778 Following
WIIM_Lethbridge @WIIM_Lethbridge
249 Followers 467 Following Providing Insurance and Investment services to Southern Alberta since 2004 -Clayton Wiest (403)380-6280
Biotech Watch @watch_biotech
56 Followers 269 Following
Candy Vandewater @CandyVandy1
140 Followers 950 Following
Julie Higgins @jhiggins28
58 Followers 211 Following
DIYAR BARKAL @dlsyr381596
7 Followers 41 Following Becker muscular dystrophy From: syria 20 years old whatsapp : +963992029169
Phillip Huber @Huber1302
4 Followers 3 Following
TheSaltyDoodle @TheSaltyDoodle
27 Followers 103 Following Keenly aware of the limits of my own knowledge and understanding.
Zlatko Todorow @todorow_zlatko
236 Followers 3K Following
HeatherHay @HeatherSWHay
4 Followers 2 Following
Marit Sivertson @MaritSivertson
15 Followers 327 Following
Tracy Elliott @TracyWa90714251
89 Followers 945 Following
John Harvey @SSebokeng50767
66 Followers 837 Following Neurosurgeon 👨⚕️ “I never dreamed about success. I worked for it.
Danielle @dhbeautycounter
20 Followers 111 Following
Partnership to Fight .. @pfcd
2K Followers 2K Following News and information on the fight against the number one cause of death, disability, and rising health care costs: chronic disease.
Eliza - DMD'yi birlik.. @ElizDem19201982
1K Followers 3K Following İlerleyici bir kas erimesi hastalığı olan DMD ile mücadele eden çocukların yaşam sevinci hiç tükenmesin! #destekolDMDyiyenelim
Beto Ocasio Cortez Jr.. @ad26201
211 Followers 749 Following Twitter claim to fame: blocked by Joe Scarborough Nicole Wallace and Rosie O’Donnell (liberals are sometimes upset by facts). Follow me, I find me amusing.
Alkhaled Mohammed م�.. @alkhaledsa
110K Followers 3K Following كاتب سعودي 🇸🇦 مدير المركز الإعلامي بنادي الخلود السعودي @alkholoodclub
Adrian Layt 🏇 @adrianlayt
3K Followers 2K Following Jockey 🏇 Father of 3 boy's 💚💚💚and an amazing young woman 👩⚖️
Duchenne UK @DuchenneUK
5K Followers 953 Following Duchenne UK has one clear aim – to end Duchenne, a devastating muscle-wasting disease. We are the leading Duchenne muscular dystrophy charity in the UK.
Lesley @Weggster
3K Followers 3K Following Seem to have lost 3 or 4 decades judging by my playlist. Music junkie. End Duchenne Muscular Dystrophy. #MusicTwitter #ActionForAshley. #HollywoodGlitterBall
Muscles for Mitchell @myboymitchell
559 Followers 617 Following Mitchell is 14. He lives with Duchenne MD. Life is for living. Make it matter. #musclesformitchell. Tweets by mum @drkatetherapy
Prof. Toshi Yokota Ph.. @ToshifumiYokota
5K Followers 5K Following Garrett Cumming @MD_Canada Chair&Prof #Antisense #RNA #CRISPR #RareDiseases #Muscle #Bone #Neurology Trained @UTokyo_News @NCNP_pr @ImperialMed @ChildrensNatl
Muscular Dystrophy As.. @MDAorg
21K Followers 2K Following MDA is the #1 voluntary health organization in the United States for people living with #MuscularDystrophy, #ALS, and related #neuromuscular diseases.
Peter J. Pitts @PeterPitts
2K Followers 538 Following President, Center for Medicine in the Public Interest, Former FDA Associate Commissioner
Joe @Gantosj
12K Followers 243 Following Equity market consultant. Technical Analysis Trader with over 25 years of experience. #Biotech Deep dive research. Biotech Trading Analyst @ChimeraResearch
World Orphan Drug Con.. @OrphanConf
5K Followers 842 Following Get regular updates on the World Orphan Drug Congress! April 23-25, 2024 | Boston Convention & Exhibition Center #WorldOrphanUSA
steve usdin @steveusdin1
3K Followers 437 Following Washington Editor, BioCentury. Author: Bureau of Spies & Engineering Communism.
Town of Darien CT @TownofDarienCT
1K Followers 59 Following Official Account of the Town of Darien, CT
IRDiRC @irdirc
3K Followers 2K Following #IRDiRC is a consortium of #RareDisease #research funding agencies n stakeholders. RTs shares likes ≠ endorsement. Account managed by IRDiRC Scient. Secretariat
Jason Mast @Jasonmmast
4K Followers 3K Following Writing about science, medicine & business for @statnews Email me: [email protected]
Fran Jones @Frannie_JoJo
7K Followers 7K Following Here to save our rights!! #ProChoice #VoteBlue, #ConnectBlue, #FBR, #LGBTQIA+, #Resist, #StrongerTogether NO DMs!
Alexa @alexaaaCT
974 Followers 4K Following Comms/social/advocacy. Opinions mine. Be smart, be thoughtful, be generous. she/her #GunControlNow #LGM
Connecticut Examiner @ctexaminer
3K Followers 4K Following Connecticut's award-winning source for state and local news -- 235,000 readers and counting. Write to us: [email protected]
Elijah Stacy @Elijahjstacy
379 Followers 250 Following Author, Public Speaker, and Founder of Destroy Duchenne. Media/bookings: [email protected]. Get my new book now 👇
Institute for Gene Th.. @gene_therapies
2K Followers 415 Following Gene therapy is transforming how we treat diseases. But today’s healthcare system can’t realize its potential. We’re changing that.
Katalin Kariko @kkariko
70K Followers 263 Following I am a scientist, working on the therapeutic use of in vitro transcribed mRNA.
Code Biotherapeutics @CodeBioTx
127 Followers 398 Following Code Bio is developing transformational, non-viral, genetic medicines to treat and potentially cure serious and life-threatening diseases.
Marit Sivertson @MaritSivertson
15 Followers 327 Following
Phillip Huber @Huber1302
4 Followers 3 Following
Partnership to Fight .. @pfcd
2K Followers 2K Following News and information on the fight against the number one cause of death, disability, and rising health care costs: chronic disease.
Hawken Miller @HawkenMiller
690 Followers 1K Following Content strategist @CureDuchenne, fmr features writer @bionewsservices, contributor @LauncherWP | hawkenmiller at gmail dot com. 💗🎮♿✝
Lesley @Weggster
3K Followers 3K Following Seem to have lost 3 or 4 decades judging by my playlist. Music junkie. End Duchenne Muscular Dystrophy. #MusicTwitter #ActionForAshley. #HollywoodGlitterBall
Victoria Arlen @Arlenv1
27K Followers 596 Following ESPN / ANWjr Host | Speaker | Gold Medalist | Victoria’s Victory Foundation Founder | Author | 💗✌🏼✝️ 🙏🏼 Philippians 4:13
Duchenne UK @DuchenneUK
5K Followers 953 Following Duchenne UK has one clear aim – to end Duchenne, a devastating muscle-wasting disease. We are the leading Duchenne muscular dystrophy charity in the UK.
Prof. Toshi Yokota Ph.. @ToshifumiYokota
5K Followers 5K Following Garrett Cumming @MD_Canada Chair&Prof #Antisense #RNA #CRISPR #RareDiseases #Muscle #Bone #Neurology Trained @UTokyo_News @NCNP_pr @ImperialMed @ChildrensNatl
WMS @WorldMuscleSoc
2K Followers 663 Following We invite you to the 28th International Annual Congress of the World Muscle Society in 2023. This is the premier annual Congress on #neuromuscular disorders.
Muscular Dystrophy As.. @MDAorg
21K Followers 2K Following MDA is the #1 voluntary health organization in the United States for people living with #MuscularDystrophy, #ALS, and related #neuromuscular diseases.
Mary Fiance @MaryFiance
554 Followers 3K Following VP, PR @MDAorg | #RareDisease, #MuscularDystrophy, #NMD, #ALS, #PR | NYC | Previously @92Y, @jazzdotorg @LincolnCenter #ViewsAreMyOwn
MDA Advocacy @MDA_Advocacy
2K Followers 316 Following MDA's Advocacy empowers the voice of the @MDAorg community & protects the interests of those we serve.
Ryan Farrell @OJnotmilk
20 Followers 91 Following
Sam Ghali, M.D. @EM_RESUS
565K Followers 274 Following ER Doctor | Resuscitation | Airway | Cardiovascular Emergencies | ECGs | Emergency Radiology | Trauma | Critical Care | #FOAMed | Patient Advocate
Aaron S. Zelikovich, .. @aszelikovich
3K Followers 985 Following @WCMCNeurology PGY-4 || @PennNeurology Neuromuscular Fellow 2024-2025 || #MedEd || Clinical Trials || #NeuroTwitterNetwork ||
Angelica Peebles @angelicapeebles
6K Followers 5K Following Pharma reporter at CNBC | Past: Biotech at Bloomberg | Formerly LaVito | Opinions my own
Parent Project Muscul.. @ParentProjectMD
7K Followers 1K Following Let's fight for every future. #PPMDeveryfuture #EndDuchenne
Genna Shapiro @GennaShapiro
155 Followers 977 Following
Sarepta Therapeutics @Sarepta
5K Followers 62 Following Commercial-stage biopharma company focused on the discovery & development of precision genetic medicine to treat rare neuromuscular diseases. https://t.co/HFP4txOCxe
Muscles for Mitchell @myboymitchell
559 Followers 617 Following Mitchell is 14. He lives with Duchenne MD. Life is for living. Make it matter. #musclesformitchell. Tweets by mum @drkatetherapy
Jett Foundation @JettFoundation
2K Followers 1K Following Empowering families. Fighting Duchenne muscular dystrophy. #FightDMDTogether
Mark Hagen @mhagen02
158 Followers 380 Following
Nina Badzin @NinaBadzin
5K Followers 429 Following Podcast host—DEAR NINA: Conversations About Friendship. I’ve been writing about friendship since 2014. Quoted in WSJ, WashPost, Chicago Trib, Guardian, StarTrib
Tori Fletcher @hellotorifletch
10K Followers 11K Following Honestly, if it were “raining men” Hallelujah wouldn’t be the word that came to mind | Part Antagonist, Part Protagonist | Usually Making Fun of my Husband
Samuel Mackenzie MD P.. @NotoriousEMG
645 Followers 487 Following Pediatric #neuromuscular doc, amateur scientist @URneuroscience, runner, chess enthusiast, dad. #Meliora
LabTenant @labratorytenant
377 Followers 100 Following Current interests include gene editing and avoiding wildfires. I delete most of my tweets because I hate surprises.
FrogFish @love2scuba_f
209 Followers 330 Following
Kathryn Doran @DoranKathryn
2K Followers 2K Following Mother, Wife, Professional Volunteer, Dog Whisperer, Breast Cancer Ass Kicker, Tired. Proud Dem. Views and statements are my own.
Ja Hish @yachmod
118 Followers 123 Following In Lebanese culture, an insult, mostly in fun, is to the English word 'jackass'. Cousin: “Help me carry these bags jahish( or also “ya kmar” aka donkey)”?
Heather King @HK_gene_targets
315 Followers 562 Following Cell+gene therapy fan. Prv: biotech comms/IR (DTIL), drug discovery open science (SGC), research folio analysis (NIH), medical research (PhD, Rockefeller)
Josh @4dmdcure
386 Followers 210 Following Father to 3 amazing kids. 21-year-old son lives with Duchenne muscular dystrophy. Passionate patient advocate, MBA, biotech investor, & marathoner.
Susan Matesanz @suzmatMD
312 Followers 516 Following mom/ child neurologist / neuromuscular / gene therapy 💪🏻🧠@childrensphila. Philadelphia, PA. All opinions are my own.
Alan Chaulet ♿✈ @AlanChaulet
1K Followers 5K Following @allwheelsup VP and Founding Board Member | @ParentProjectMD PAAC I #BentleyU Grad I DMD and Disability Advocate | All Views My Own |
Learn about the latest advancements in genetic medicine for eligible patients.
Apparently, Happy Meals will not be served during the Revolution. #FeedMe
Reporter grills Columbia student after she demands the university help feed protestors occupying Hamilton Hall: "It seems like you're saying, 'we want to be revolutionaries, we want to take over this building, now would you please bring us some food'."
I don’t know who needs to hear this but your kid does not need that teepee.
This from @AMarch4OurLives is deeply upsetting and misinformed. March for Our Lives as a group exists because of what happened in the Parkland shooting where my daughter and 16 others were murdered. Back then they held protests and marches that were peaceful, just, and…
So they unlawfully take over a building on campus and occupy it, but want the school to let Uber Eats and Door Dash thru? Help me folks. 🤷🏽♂️
Reporter grills Columbia student after she demands the university help feed protestors occupying Hamilton Hall: "It seems like you're saying, 'we want to be revolutionaries, we want to take over this building, now would you please bring us some food'."
The level of entitlement amongst these terrorists sympathizing kids who are destroying campus property is unbelievable. If they want food while they pursue their antisemitism, tell them to call Door Dash and request a non Jewish driver.
Reporter grills Columbia student after she demands the university help feed protestors occupying Hamilton Hall: "It seems like you're saying, 'we want to be revolutionaries, we want to take over this building, now would you please bring us some food'."
He glared at me on the way out of the courtroom for the mid-morning break. I grinned at him.
$SRPT (and friends) More and more I believe the skippers will remain highly relevant. “In treatment of patients with single-exon duplications, these agents may have advantages over alternative approaches, such as microdystrophin." #casimersen #golodirsen 💪rarediseaseadvisor.com/news/potential…
So many characterize @MSNBC as unwatchable between 12-4 pm. Exhibit A:
@Halcyon270 @MSNBC Katy Tur just came within a hair’s breadth of defending trump’s abysmal record as pres because he had the misfortune of being in charge during the pandemic. Speaker Pelosi flared “you may choose the role of apologist for Donald trump, but it’s sure not mine!” What’s up with/Katy?
@atrupar Madame Speaker takes no prisoners! I love it. It’s about time someone put Katy Tur in her place.
@atrupar Hey Nancy - do Andrea Mitchell next!
@atrupar Good for Nancy Pelosi! @TeamPelosi
Happy 91st birthday Willie Nelson! Big thanks to you and Annie for your support, confidence in science, and inspiration. Keep on rocking and inspiring us all! @UTSWMedCenter @BioAnnie2 @WillieNelson
All of my social media feeds are filled with these videos of Mother’s Day cards that explode open and spread whimsical paper items everywhere and yes, of course, let’s gift Mom something that makes a big mess, you know how much she loves those
Exciting news! Our article on Antisense and Gene Therapy Options for Duchenne Muscular Dystrophy Arising from Mutations in the N-Terminal Hotspot has been featured as a highly cited paper on the @Genes_MDPI homepage. Check it out! mdpi.com/journal/genes/… mdpi.com/2073-4425/13/2…
Made Sesame Tofu & Broccoli for dinner New recipe Called for something called "chili crisp" I had never cooked with that It is hot as shit I may not survive this my head is sweating and I think I perforated my esophagus My last words can be "don't use so much chili crisp"
Back in March, @JoeBiden, @BillClinton and I sat down with three real icons – the hosts of @SmartLess – to talk about everything from the economy and gun violence, to what we miss about being in office and the importance of sending Joe and Kamala back to the White House. We…
On our first triple-guest podisode, we let our pal President @JoeBiden bring along two friends, Former Presidents @BarackObama and @BillClinton. Let’s get a little less-SmartLess together… on an all new @SmartLess. @SeanHayes @batemanjason @arnettwill
Hell have no fury like a toddler scorned because they didn’t push the elevator button first 🤦🏻♂️
I like this guy.
This is the start of Keon Coleman's first press conference as a member of the Buffalo Bills. Covering this man is going to be a real treat. #BillsMafia @WKBW
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